The United States has approved breakthrough gene editing therapy using the CRISPR tool to treat sickle cell disease. This is a major advancement in gene therapy for patients with sickle cell disease, which affects over 100,000 Americans, mostly Black individuals. The therapy was approved by the US Food and Drug Administration and uses Nobel Prize-winning CRISPR technology. The potential to transform the lives of patients with sickle cell disease is enormous. CRISPR, a precise gene editing technique, has revolutionized molecular life studies and has been approved for use in gene therapy in the UK as well. This breakthrough offers hope for those suffering from this debilitating and life-threatening illness.
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US approves sickle cell breakthrough with gene editing therapy
