New research from Italy shows that children born with type 1 spinal muscular atrophy after 2016 had better outcomes and survival rates compared to those born before then. Of the 241 children born with type 1 SMA since 2016, 199 were still alive at the time of the last follow-up. Disease-modifying therapies have significantly improved survival rates for these children, with 65% achieving independent sitting and 87.9% no longer requiring tube feeding. In comparison, 69% of children born with type 1 SMA between 2010 and 2015 died. The study highlights the positive impact of new therapies on the outcomes of children with SMA.
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Children born with spinal muscular atrophy from 2016 on are living longer
